The final decision now rests with the FDA itself.

October 13, 2017

It would be the first treatment in the U.S. that fixes an inherited genetic trait.

October 12, 2017

We need to make this happen.

October 6, 2017

Their novel gene therapy method makes retinal cells sensitive to light.

October 3, 2017

It could end the need for children to undergo painful surgeries.

September 15, 2017